Treatment introduces an expansion of the scope of gene therapies that might lead to similar treatments for neurodegenerative ...
In a preclinical study, UC Davis Comprehensive Cancer Center scientists have developed a highly targeted gene therapy that ...
After years of heartbreak, researchers have found an experimental treatment that can slow the progression of Huntington’s ...
A gene-editing therapy led to durable changes in serum transthyretin levels among people with hereditary transthyretin ...
Groundbreaking study demonstrates that targeted oligodendrocyte gene therapy leads to decreased N-acetylaspartate (NAA) levels and increased ...
T cell therapy, which uses a patient's own immune cells to fight cancer, has emerged as a powerful way to treat lymphoma and ...
A one-time gene therapy called AMT-130 helped slow the progression of Huntington's disease by 75%, paving the way for the ...
The first participant in an investigational gene therapy trial of STXBP1 encephalopathy died, Capsida Biotherapeutics said. The death occurred days after dosing, according to information posted on the ...
A team led by scientists at Harvard Medical School, Massachusetts General Hospital, and the Broad Institute of MIT and ...