The FDA letter requested that a technical information update be included in the Chemistry Manufacturing and Controls (CMC) ...

The FDA in September issued two rejections for spinal muscular atrophy therapies—both linked to manufacturing problems—and ...

A new international study has shown that treating babies with spinal muscular atrophy before symptoms appear can dramatically improve outcomes.Emily ...

In recent years, the U.S. Food and Drug Administration (FDA) has approved a wave of new therapies, including gene therapies, ...

Not sure how to bring up a treatment change with your SMA doctor? Learn communication tips, key questions to ask, and a ...

This mass poisoning is suspected to have originated from processed skipjack tuna on the free meals menu on Wednesday ...

The end of the earnings season is always a good time to take a step back and see who shined (and who not so much). Let’s take ...

The FDA has rejected apitegromab as a treatment for spinal muscular atrophy due to issues at a manufacturing facility.

Influencer and reality TV personality Juan ‘Raymond’ Harper, known as Rolling Ray, has died at the age of 28, days before his 29th birthday. Ray rose to internet fame with comedy skits before later ...

Detailed price information for Ionis Pharmaceuticals (IONS-Q) from The Globe and Mail including charting and trades.

Mother of two, Kasey Mumford, 24, from Warwick, gave birth to her second child, Chester, last August. Her mother’s intuition ...

Columnist G Shellye Horowitz used to be skeptical of AI, but a recent experience opened her eyes to the tool's potential in ...