Stealth BioTherapeutics has claimed FDA approval for Forzinity, the first treatment for ultra-rare disease Barth syndrome, ...
Elderly residents of Porepunkah have had their home nurse visits cancelled as alleged police killer Dezi Freeman remains at large.
BACKGROUND: PYGM (muscle glycogen phosphorylase), the rate-limiting enzyme in glycogenolysis, plays an indispensable role in maintaining cardiac energy metabolism. However, the role of PYGM in the ...
When doctors prescribe oxybutynin, it's usually for an unglamorous problem: bladder incontinence. But researchers have discovered a surprising new role for this decades-old drug—one that could open ...
Robert F. Kennedy Jr.'s recent claims about diagnosing mitochondrial issues in children simply by observing their faces and posture have sparked controversy. While he emphasizes the importance of ...
Inherited metabolic diseases are rare monogenic conditions that disrupt biochemical pathways, affecting energy production and ...
The Company is currently seeking a path forward with the FDA that would not require an additional clinical trial. The Food and Drug Administration (FDA) has issued a Complete Response Letter (CRL) to ...
Muscular Dystrophy UK, a charity working on behalf of 110,000 children and adults living with more than 60 muscle-wasting conditions, has awarded £140,944 in funding to Dr. Rebecca Jones at Aston ...
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